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Uniparental disomy (UPD) is a rare phenomenon in which both copies of a chromosome are inherited from a single parent. This can lead to genomic imprinting disorders and recessive disorders due to the presence of recessive pathogenic variants in both alleles. Additionally, depending on the mechanisms by which UPD occurs, mosaic aneuploidies may arise. Here we report the case of a patient with prenatal manifestations of intrauterine growth restriction and polyhydramnios, and postnatal manifestations of multiple congenital anomalies, developmental delay, and facial dysmorphisms. Prenatal exome sequencing targeting the fetal phenotype allowed the detection of uniparental isodisomy of chromosome 19. After birth, exome reanalysis revealed a homozygous pathogenic variant in the PEPD gene. This is the first case of prolidase deficiency due to UPD ever described. Prolidase deficiency is a low-prevalence disease with significant morbidity and mortality. Early diagnosis is essential to provide prognostic information, design an appropriate interdisciplinary follow-up program, and anticipate complications. This case highlights the importance of phenotypic assessment and postnatal clinical follow-up, as well as comprehensive genetic analyses to better understand complex phenotypes.
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http://dx.doi.org/10.1002/ajmg.a.64125 | DOI Listing |
J Dermatol
August 2025
Department of Dermatolog, Y, Kanazawa Medical University, Uchinada, Ishikawa, Japan.
Mol Genet Metab
July 2025
Department of Metabolic Disease, Wilhelmina Kinderziekenhuis Utrecht, University Medical Centre Utrecht, Utrecht, the Netherlands. Electronic address:
Prolidase deficiency is an ultra-rare metabolic disorder caused by pathogenic variants in the PEPD gene, which causes a wide range of symptoms including chronic ulcers, recurrent infections, systemic lupus erythematosus (SLE), facial dysmorphisms and developmental delay. How decreased prolidase activity - thus an inability to cleave C-terminal proline imidodipeptides - eventually causes these symptoms is as yet poorly understood. However, recent research has unveiled additional roles of prolidase in cellular homeostasis, including regulation of important signalling molecules such as TGF-β, VEGF and p53.
View Article and Find Full Text PDFAm J Med Genet A
October 2025
Quantitative Genomic Medicine Laboratories (qGenomics), Esplugues de Llobregat, Barcelona, Spain.
Uniparental disomy (UPD) is a rare phenomenon in which both copies of a chromosome are inherited from a single parent. This can lead to genomic imprinting disorders and recessive disorders due to the presence of recessive pathogenic variants in both alleles. Additionally, depending on the mechanisms by which UPD occurs, mosaic aneuploidies may arise.
View Article and Find Full Text PDFJ Clin Immunol
February 2025
Respiratory Department II, National Clinical Research Center for Respiratory Diseases, Beijing Children's Hospital, Capital Medical University, National Center for Children's Health, NO.56, Nanlishi Road, Beijing, 100045, China.
Turk Arch Pediatr
January 2025
Division of Allergy and Immunology, Department of Pediatrics, Marmara University Faculty of Medicine, İstanbul, Türkiye.
Objective: Prolidase deficiency is a metabolic and immunological disorder that is inherited in an autosomal recessive manner. In prolidase deficiency, a broad spectrum of differences is observed in patients, ranging from asymptomatic to multisystem involvement. There is scarce information in the literature on the atypical features and immunophenotypes of this disease.
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